Cereno Scientific has reported initial long-term safety findings from a [...]
City St George’s, University of London has partnered with Paradigm [...]
A new global initiative aims to address long-standing limitations in [...]
Efzimfotase alfa shows mixed Phase 3 results in hypophosphatasia across pediatric and adult patients
Efzimfotase alfa has shown positive Phase 3 results in children [...]
BridgeBio Pharma has submitted a New Drug Application (NDA) to [...]
Chiesi Global Rare Diseases has received a positive CHMP opinion [...]
Levicept has reported Phase 2 clinical trial results for LEVI-04 [...]
The US Food and Drug Administration (FDA) has reaffirmed that [...]
Tozorakimab has met its primary endpoint in two replicate Phase [...]
FoRx Therapeutics presents preclinical data on FORX-428, a PARG inhibitor [...]