As Rare Disease Day 2026 shines a spotlight on patients [...]

Cereno Scientific has completed the last patient’s last visit in [...]

Kedrion has received orphan drug designation from the European Medicines [...]

Minovia Therapeutics has received orphan drug designation from the US [...]

Barcelona-based biotech advances Huntington’s programme as EMA backs orphan designation, [...]

Selection of CRO marks key milestone in advancing CS1 as [...]

Dosing of CPV-104 in healthy volunteers marks key milestone in [...]

Poolbeg Pharma has been granted Orphan Drug Designation (ODD) by [...]

Kaerus Bioscience has been granted Orphan Drug Designation and Rare [...]