Genespire has started enrolling children with severe methylmalonic acidemia in [...]

The FDA has accepted Belite Bio’s application for tinlarebant and [...]

Vaderis Therapeutics has raised $152M and started a global Phase [...]

Zilucoplan has been accepted for restricted use in NHS Scotland [...]

Grifols has completed patient follow-up in its Phase 3 SPARTA [...]

Amorphical has completed patient enrolment in a Phase 2 trial [...]

Medicus Pharma has received FDA clearance to begin a Phase [...]

CAMP4 Therapeutics has received Australian regulatory and ethics clearance to [...]

The EMA’s CHMP has recommended approval of NEZGLYAL for boys [...]

Skyhawk Therapeutics has expanded its global pivotal Phase 2/3 clinical [...]